A mother is speaking out in hopes of helping other parents after her 11-week-old baby was diagnosed with botulism. The ...

The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...

A 10-month-old baby who sparked nationwide headlines after receiving a first-of-its kind gene-editing treatment was released ...

RENSSELAER, N.Y. (NEWS10) — A child in Rensselaer is battling a rare disease that will affect her speech, mobility and doctors said she is only expected to live to her late teens or early 20s. Her ...

Baby battling rare disease in Rensselaer; family asking for help Video A child in Rensselaer is battling a rare disease that will affect her speech, mobility and eventually could cause her to die by ...

AGC Biologics Partners with Rarity PBC to Advance Life-Saving Gene Therapy for "Bubble Baby Disease" Collaboration will leverage AGC Biologics’ commercial manufacturing experience and proven platforms ...