A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...
New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
In a study published in Nature Medicine, Leone and her team reported the first targeted gene therapy to restore myelin, the ...
Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...
A blood stem cell gene therapy co-developed by UCLA’s Dr. Donald Kohn restored immune function in 59 of 62 children with ADA-SCID, a rare and fatal immune disorder, with no serious complications ...
Fractyl Health announced a first-in-human trial for RJVA-001, targeting T2D and obesity, pending regulatory approval by 2026. Fractyl Health, Inc. has announced the submission of the first module of ...
Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct gene-editing experiments. The device, CRISPR-GPT, is an artificial intelligence lab ...
The race to advance gene editing tech continues, spurred on by starry-eyed Silicon Valley investors, entrepreneurs and even ...