Add Yahoo as a preferred source to see more of our stories on Google. Actor Colin Farrell recently disclosed that his son, James, has Angelman syndrome, one of the driving factors behind Farrell's ...

The recent FDA approval of Fayuvi for a rare, childhood neurodegenerative disease was “particularly special” for Ultragenyx ...

Add Yahoo as a preferred source to see more of our stories on Google. The rare neurogenetic disorder affects 1 in 15,000 people For the first time, Colin Farrell has opened up his home and talked ...

AS2Bio: MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today announced that the U.S. Food and Drug ...

Phase 3 Aspire did not achieve the primary endpoint of change from Baseline in Bayley-4 cognitive raw score nor the key secondary endpoint of net response in Multidomain Responder Index (MDRI) NOVATO, ...

Colin Farrell says his personal life has inspired him to launch a new foundation aimed at helping people with intellectual disabilities. The actor, 48, recently launched the Colin Farrell Foundation, ...

Angelman syndrome affects roughly 1 in every 20,000 children and it has no approved treatment. Researchers recently published results of early tests of a gene therapy strategy for Angelman syndrome, a ...

Actor Colin Farrell, long an advocate for people with intellectual disabilities, has started a foundation in honor of his son, James, who suffers from Angelman syndrome, a rare neurogenetic disorder.

UConn researchers Stormy Chamberlain and Noelle Germain are working with biopharmaceutical company Ovid Therapeutics Inc. on a promising therapy for a rare genetic condition. Families visit Stormy ...

Angelman syndrome is a genetic disease with no cure. Children grow up with severe intellectual disabilities and a range of other problems, arguably the worst of which are epileptic seizures. Now ...

Babies born with a faulty maternal copy of the UBE3A gene will develop Angelman syndrome, a severe neurodevelopmental disorder with no cure and limited treatments. Now, for the first time, scientists ...